Better Care for Rare
Find out about our commitment to faster diagnoses, sustainable access, and integrated patient support in rare diseases
Better Care for Rare
Therapeutic areas within Rare Diseases
Get more familiar with the science of rare diseases. Learn about pathophysiology, testing and treatments, including specialised care services
Fabry Disease
Pompe Disease
MPS I Disease
Gaucher Disease
Rare Diseases Products

Prescribing Information GB
Prescribing Information NI
MAT-XU-2200954 (v2.0)
Date of preparation: February 2023

Prescribing Information GB
Prescribing Information NI
MAT-XU-2204064 (v2.0)
Date of preparation: January 2023

Prescribing Information GB
Prescribing Information NI
MAT-GB-2105812 (v3.0)
Date of preparation: February 2023

Prescribing Information GB
Prescribing Information NI
MAT-XU-2204065 (v2.0)
Date of preparation: January 2023
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Prescribing Information GB
Prescribing Information NI
MAT-GB-2105179 (v3.0)
Date of preparation: February 2023

NEXVIADYME
avalglucosidase alfa
Prescribing Information GB
GB ONLY CONTENT
MAT-XU-2203480 (v3.0)
Date of preparation: February 2023
- Rare Diseases. National Center for Advancing Translational Sciences. Available at: https://www.raredisease.org.uk/media/1588/the-rare-reality-an-insight-into-the-patient-and-family-experience-of-rare-disease.pdf Accessed August 2022.
MAT-GB-2105722 (v4.0)
Date of preparation: February 2023