Better Care for Rare

Find out about our commitment to faster diagnoses, sustainable access, and integrated patient support in rare diseases

Better Care for Rare

Therapeutic areas within Rare Diseases

Get more familiar with the science of rare diseases. Learn about pathophysiology, testing and treatments, including specialised care services

Fabry Disease

Pompe Disease

MPS I Disease

Gaucher Disease

Rare Diseases Products

ALDURAZYME
laronidase

Prescribing Information GB
Prescribing Information NI

 

MAT-XU-2200954 (v2.0)
Date of preparation: February 2023

CERDELGA
eliglustat 84mg

Prescribing Information GB
Prescribing Information NI

MAT-XU-2204064 (v2.0)
Date of preparation: January 2023

Fabrazyme
agalsidase beta

Prescribing Information GB
Prescribing Information NI

 

MAT-GB-2105812 (v3.0)
Date of preparation: February 2023

CEREZYME
imiglucerase

Prescribing Information GB
Prescribing Information NI

 

MAT-XU-2204065 (v2.0)
Date of preparation: January 2023

MYOZYME
alglucosidase alfa

Prescribing Information GB
Prescribing Information NI

MAT-GB-2105179 (v3.0)
Date of preparation: February 2023

NEXVIADYME
avalglucosidase alfa

Prescribing Information GB
GB ONLY CONTENT

 

MAT-XU-2203480 (v3.0)
Date of preparation: February 2023

    1. Rare Diseases. National Center for Advancing Translational Sciences. Available at: https://www.raredisease.org.uk/media/1588/the-rare-reality-an-insight-into-the-patient-and-family-experience-of-rare-disease.pdf Accessed August 2022.

MAT-GB-2105722 (v4.0)
Date of preparation: February 2023