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후기 발병형 폼페병 환자의 평가측정도구 개발 : Modified Rasch-Built Pompe-Specific Activity scale

후기 발병형 폼페병 환자의 평가측정도구 개발 : Modified Rasch-Built Pompe-Specific Activity scale

Improving outcome measures in late onset Pompe disease: Modified Rasch-Built Pompe-Specific Activity scale
van Kooten HA, et al. Eur J Neurol. 2024:e16397

치료 경험이 없는 후기 발병형 폼페병 성인 환자에서 avalglucosidase alfa와 alglucosidase alfa 투여 후 치료 결과 비교: 3상 COMET 연구 사후분석

치료 경험이 없는 후기 발병형 폼페병 성인 환자에서 avalglucosidase alfa와 alglucosidase alfa 투여 후 치료 결과 비교: 3상 COMET 연구 사후분석

Effect of avalglucosidase alfa on disease-specific and general patient-reported outcomes in treatment- naïve adults with late-onset Pompe disease compared with alglucosidase alfa: Meaningful change analyses from the Phase 3 COMET trial
Toscano A, et al. Mol Genet Metab. 2024;141(2):108121.

프랑스의 폼페병 레지스트리를 활용한 후기 발병형 폼페병 환자의 bulbar muscle impairment 분석

프랑스의 폼페병 레지스트리를 활용한 후기 발병형 폼페병 환자의 bulbar muscle impairment 분석

Bulbar muscle impairment in patients with late onset Pompe disease: Insight from the French Pompe registry
Retailleau E, et al. Eur J Neurol. 2024;31(10):e16428.

Estudios relevantes sobre el C-LDL y el riesgo cardiovascular​

Estudios relevantes sobre el C-LDL y el riesgo cardiovascular​

Conozca en esta cápsula algunos de los insights más importantes de los estudios relevantes sobre el C-LDL y el riesgo cardiovascular.

Factores de riesgo de la enfermedad cardiovascular​

Factores de riesgo de la enfermedad cardiovascular​

Profundice en esta cápsula sobre los factores de riesgo de la enfermedad cardiovascular​

ERT infusions management

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