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Inflamación Tipo 2, uno de los principales Impulsores de la disfunción olfativa por la Dra. Cuevas

La Dra. Cuevas aborda el rol de la Inflamación Tipo 2, un factor clave detrás de la disfunción olfativa. Descubre cómo esta inflamación impacta el sentido del olfato y qué soluciones innovadoras están transformando el manejo de los pólipos nasales.

D-dimery a jejich využití v klinické praxi

Toujeo - studie BRIGHT

Kazuistika - iniciace léčby inzulínem Toujeo

후기 발병형 폼페병 환자의 평가측정도구 개발 : Modified Rasch-Built Pompe-Specific Activity scale

Improving outcome measures in late onset Pompe disease: Modified Rasch-Built Pompe-Specific Activity scale
van Kooten HA, et al. Eur J Neurol. 2024:e16397

치료 경험이 없는 후기 발병형 폼페병 성인 환자에서 avalglucosidase alfa와 alglucosidase alfa 투여 후 치료 결과 비교: 3상 COMET 연구 사후분석

Effect of avalglucosidase alfa on disease-specific and general patient-reported outcomes in treatment- naïve adults with late-onset Pompe disease compared with alglucosidase alfa: Meaningful change analyses from the Phase 3 COMET trial
Toscano A, et al. Mol Genet Metab. 2024;141(2):108121.

프랑스의 폼페병 레지스트리를 활용한 후기 발병형 폼페병 환자의 bulbar muscle impairment 분석

Bulbar muscle impairment in patients with late onset Pompe disease: Insight from the French Pompe registry
Retailleau E, et al. Eur J Neurol. 2024;31(10):e16428.

ERT infusions management

ERT infusions management

ERT infusions management

ERT infusions management

ERT infusions management