Rare Disease States
Fabry
Gaucher
Pompe
MPS I and II
Latest science on rare disease
Inspiring science: What's trending?
Stay in the know with the latest trends in science and medicine worldwide through up-to-date
videos, articles and podcasts.
Resources and tools
Discover the latest resources and tools to share with your patients.
Fabry Pain Diary app
A smart phone app developed specifically to assist patients diagnosed with Fabry disease to monitor and record their pain symptoms.
Looking for ways to support your patients in rare disease?
MAT-AU-2102434: February 2022