Rare Disease States




MPS I and II

Inspiring science: What's trending?

Stay in the know with the latest trends in science and medicine worldwide through up-to-date
videos, articles and podcasts.

Resources and tools

Discover the latest resources and tools to share with your patients.

Fabry Pain Diary app

A smart phone app developed specifically to assist patients diagnosed with Fabry disease to monitor and record their pain symptoms.

Looking for ways to support your patients in rare disease?

MAT-AU-2102434: February 2022